| Disease Name | Target Genes | Targeting Methods | Ordering |
| Spinal muscular atrophy, SMA | Smn1 | Humanization | Order Now |
| Smn2 | KI | Order Now | |
| Frontotemporal dementia, FD | Mapt | Humanization(WT, Mu) | Order Now |
| Spinocerebellar ataxia, SCAs | Atxn3 | Humanization(WT, Mu) | Order Now |
| Familial dysautonomia, FD | Elp1 | Humanization(WT, Mu) | Order Now |
| Spinal muscular atrophy with respiratory distress type 1, SMARD1 | Ighmbp2 | Humanization(WT, Mu) | Order Now |
| Parkinson's disease, PD | Snca | Humanization(WT, Mu) | Order Now |
| Lrrk2 | Mu | Order Now | |
| Amyotrophic lateral sclerosis, ALS | Tardbp | Humanization(WT, Mu) | Order Now |
| Fus | Humanization(WT, Mu) | Order Now | |
| Sod1 | TG | Order Now | |
| Huntington's disease, HD | Htt | TG | Order Now |
| Rett syndrome | Mecp2 | Humanization(WT, Mu) | Order Now |
| Cornelia de Lange syndrome, CdLS | Nipbl | KO | Order Now |
| Gaucher disease, GD | Gba | CKO | Order Now |
| Niemaoh-Pick disease, NPD | Npc1 | CKO | Order Now |
| Hereditary spastic paraplegia 2, HSP2 | Plp1 | CKO | Order Now |
| Joubert syndrome, JS | Ahi1 | CKO | Order Now |
| Angelman syndrome, AS | Ube3a | KO | Order Now |
| Friedreich's ataxia, FRDA | Fxn | KO | Order Now |
| Metachromatic leukodystrophy, MLD | Arsa | KO | Order Now |
| GM1 gangliosidosis, GM1 | Glb1 | KO | Order Now |
| Charcot-Marie-Tooth disease, CMT | Pmp22 | TG | Order Now |
| Subacute necrotizing encephalomyelopathy, SNE | Surf1 | KO | Order Now |
| Vanishing white matter disease, VWM | Eif2b5 | Mu | Order Now |